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PA9.1-2 | Amyloidosis — Summary & Reflection

REFLECT

Take 3–4 minutes before reading the summary.

  1. Without looking back, classify the following into AL, AA, ATTR, or localised: (a) A dialysis patient with carpal tunnel syndrome; (b) a 60-year-old man with myeloma and macroglossia; (c) an elderly man with echocardiographic hypertrophy and low ECG voltage; (d) medullary thyroid carcinoma stroma.
  1. A colleague says, "All amyloid looks the same on H&E — why bother typing it?" Draft a 2-sentence rebuttal explaining why protein typing changes management.
  1. Why is the abdominal fat pad the preferred first biopsy site rather than the kidney, even when the kidney is clearly affected on clinical grounds?

KEY TAKEAWAYS

Amyloidosis — Core Framework

What: Extracellular deposits of misfolded proteins sharing a β-pleated sheet secondary structure. Insoluble, resistant to proteolysis.

How to recognise it:
• H&E: amorphous, homogeneous, eosinophilic extracellular hyaline material
• Congo red + polarised light: apple-green birefringence — pathognomonic
• Gross: waxy, lardaceous, enlarged firm organs

Classification by protein:

TypeProteinDisease link
ALImmunoglobulin light chainPlasma cell dyscrasia / myeloma
AASerum amyloid-associated (SAA)Chronic inflammation (RA, TB, IBD)
Aβ2Mβ2-microglobulinLong-term haemodialysis
ATTRTransthyretinFamilial (mutation) / Senile (cardiac)
Amyloid-β peptideAlzheimer disease, Down syndrome
EndocrineCalcitonin / AmylinMedullary thyroid Ca / Type 2 DM

Pathogenesis: Protein overproduction or structural instability → misfolding → β-sheet aggregation → fibril nucleation (seeding) → extracellular accumulation → pressure atrophy + ischaemia

Organs and consequences:
Kidney (most common, most lethal): nephrotic syndrome → renal failure
Heart: restrictive cardiomyopathy, ECG-echo mismatch
Spleen: sago (follicular) or lardaceous (diffuse) pattern
Tongue: macroglossia (AL hallmark)
Nerves: sensorimotor + autonomic neuropathy

Diagnosis: Abdominal fat pad aspiration (first choice) + Congo red histology; type with IHC or mass spectrometry

Treatment principle: Eliminate the source of the precursor protein